2019 Spring CMTA Report

Clinical Trials: A Primer! In addition to our regular features, read about “A Clinical Trial for Caroline,” fast tracking and more.

• A Message from CEO Amy Gray
• Welcome to the CMTA Advisory Board, Ken Cornell
• A Clinical Trial for Caroline
• Clinical Trials: A Primer
• Clinical Trials for Rare Diseases
• CMTA-Funded Research Database for CMT2 Identifies New Disease-Causing Mutations
• ACE-083 Gets Orphan Drug Designation
• Monthly Giving Benefits CMTA and Donors
• Join CMTA Innervators and Make a Lasting Difference
• CMTA and MDA Co-Fund Study on Gene Replacement Therapy for CMT1X
• From Diagnosis to Marathon to Lab in Five Months: A Patient’s Perspective
• Walk This Way: Morristown, New Jersey
• CMTA Unveils Updated Logo
• Lace-up High Tops (Self-Prescribed)
• Jim Lea’s Legacy
• Smile and Give Others Superpowers
• Have You Seen Jeana Sweeney’s New Hat?
• Don’t Fear the Chair!
• Branch Leader Spotlight: Corey Dalfrey, Southern Louisiana
• Students at Boston College High School Raise Funds for the CMTA