Development of Treatments for CMT2D

…response and the CMT symptoms improved. The drug also has benefits when treatment is started after CMT symptoms have developed, and maintaining the benefits requires continued treatment. If treatment is…

A Comprehensive Guide to Clinical Trials

…is. In a clinical trial, participants are assigned to either receive the new treatment or a placebo treatment for comparison. In the United States, trials are conducted under strict guidelines…

A New Treatment for CMT1A

DTx Pharma is directly targeting the genetic cause for CMT1A in its upcoming clinical development program. DTx Pharma is developing a treatment for CMT1A that directly targets the cause of…

Novartis Secures $1.3B Deal for CMT Treatment CKD-510

Novartis is making significant strides in the field of Charcot-Marie-Tooth (CMT) disease treatments, having recently entered into a substantial $1.3 billion deal with Chong Kun Dang Pharmaceutical Corp (CKD). The…

Charcot–Marie–Tooth ‎Disease and Breathing Problems

…CMT-related respiratory muscle weakness provides treatment challenges the general public doesn’t typically have. Successful treatment with any of these three options rests on the individual having normal respiratory muscle strength—no…