Development of Treatments for CMT2D

…response and the CMT symptoms improved. The drug also has benefits when treatment is started after CMT symptoms have developed, and maintaining the benefits requires continued treatment. If treatment is…

A Comprehensive Guide to Clinical Trials

…is. In a clinical trial, participants are assigned to either receive the new treatment or a placebo treatment for comparison. In the United States, trials are conducted under strict guidelines…

A New Treatment for CMT1A

DTx Pharma is directly targeting the genetic cause for CMT1A in its upcoming clinical development program. DTx Pharma is developing a treatment for CMT1A that directly targets the cause of…

CMT1A Ionis Press Release

New Research Shows Promise for CMT Progressive Neuromuscular Disease Potential treatment offers hope for over 2.8 million affected worldwide Glenolden PA, December 4, 2017—A new paper published December 4th on…

Data Shows Benefit with PXT3003 in Patients with CMT1A

treatments. Pharnext has two lead products in clinical development. PXT3003 completed an international Phase III trial with encouraging topline results for the treatment of Charcot-Marie-Tooth disease type 1A (‘CMT1A’) and…

Webinar Recordings

…has spent the last decade specializing in treatment of adults with acquired neurological impairments. She is certified in neuro-developmental treatment and the use of physical agent modalities. She has specialty…