CMTA and ToolGen Announce CMT1A Collaboration

CMTA and ToolGen Announce Collaboration to Develop Potential Treatment for CMT1A Using Gene Therapy (Glenolden, PA, October 7, 2021) The Charcot–Marie–Tooth Association (CMTA), the largest philanthropic funder of CMT research…

CMTA and Addex Announce CMT1A Collaboration

CMTA and Addex Therapeutics Enter Collaboration to Advance GABA B PAM as Potential Treatment for CMT1A Addex Therapeutics is a clinical-stage pharmaceutical company pioneering allosteric modulation-based drug discovery and development….

How to Contact Your Hometown Media

…be identified for early treatment. Charcot-Marie-Tooth is a progressive disorder of the peripheral nerves that causes people to lose the normal use of their feet and legs. Symptoms include: foot…

Pharnext Premier PXT3003 for CMT1A Phase 3 Study

…for CMT1A, and treatment consists of supportive care such as orthoses, physical and occupational therapy or surgery. The purpose of the PREMIER study is to discover if PXT3003 is effective…

The Summer 2021 CMTA Report

…Gray Celebrating Steve (and his 2 decades of fundraising) CMTA Awards Züchner $300,000 for Gene Discovery Work CMTA Awards $100,000 to Explore Potential 1X Treatment CMTA-STAR Awards $1.1 Million in…

All Other Types

…CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be of therapeutic benefit across a variety of CMT types. PROJECT GOAL:…

CMT2S Research

…using mouse models of several forms of CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be of therapeutic benefit across…

CMT2D Research

…Scientific Advisory Board, is using mouse models of several forms of CMT to determine which types may be candidates for treatment with HDAC6 inhibitors and whether HDAC6 inhibitors may be…

Who Inspires You to Give?

…that seeing the CMTA’s research progress and knowing that she is leaving a legacy and contributing to a treatment/cure inspires her to give. Under the CMTA’s Strategy to Accelerate Research,…