Gene Replacement Therapy in CMT4 Subtypes
…of accelerating gene replacement therapies for CMT, underscoring our leadership in this critical area of research,” said Katherine Forsey, PhD, CMTA Chief Research Officer. “This investment in gene replacement therapy…
CMTA-INC Alliance Announces 2025 Inherited Neuropathies Fellowship Recipient
…Reilly, MBE, MD, at University College London, who also serves as CMTA’s Strategy To Accelerate Research (CMTA-STAR) Clinical Expert Board Co-Chair. It aims to build long-term clinical research capacity to…
CMTA Presents New Genetic Landscape Analysis at The 2025 Annual Meeting of the Peripheral Nerve Society
…CMT4A, and CMT4C. Register With Patients as Partners in Research Today Not yet registered with CMTA’s Patients as Partners in Research? Sign up today to be among the first to…
CMTA Report_Winter 2024 – STAR Special Edition_Download
2023 CMTA Annual Report
CMTA 2023 Annual Report
Three Major Patient Advocacy Groups Focused on CMT Research Collaborating on FDA “Voice of the Patient” Report
…condition. We thank the HNF for coordinating this important meeting and the MDA for their partnership. We believe this collaboration will help accelerate research and treatments for CMT patients worldwide….
Development of Advanced Research Diagnostic Capabilities for the CMT Community
…to address this issue by aggregating genetic data (panels, exomes, and genomes) from patients into a common database. This database is available to qualified researchers in the field and this…
CMT1A Research Breakthrough!
…hopeful breakthrough for medical researchers, healthcare professionals, patients, and families. Ionis researchers used their expertise as a world leader in developing antisense oligonucleotides, which precisely target the products of genes…
Bruce R Conklin, MD Joins the CMTA STAR Advisory Board
…Advisory Board (SAB). The SAB is comprised of world-leading experts who provide scientific input and evaluation of ongoing or proposed CMTA funded research projects and guide the CMTA’s research strategy….