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CMTA Appoints Biotech Industry Veteran Suzanne Bruhn, PhD as New CEO
…treatments for rare diseases, will take the helm of the patient-led nonprofit as it moves to the next phase of its search for a cure for CMT. Dr. Bruhn brings…
CMTA Hails Novartis Acquisition of DTx Pharma And Its CMT1A Therapeutic Program
…of novel CMT treatments capable of reaching the peripheral nervous system. Under the terms of the agreement, Novartis will make an upfront payment of $500 million and additional payments of…
October 2023 Community Statement from Novartis
“The CMTA welcomes this community update from Novartis and applauds its leading role in the development of treatments for CMT. The CMTA has been maintaining regular contact, providing support and…
Understanding Charcot-Marie-Tooth Disease in Children
…no approved treatments for CMT. Understanding CMT in Children Children with CMT sometimes take longer to reach physical milestones, such as walking, hopping, jumping with two feet, or getting up…
CMT4 Research
…the treatment of monogenic diseases of the central nervous system (CNS) in both rare and large patient populations, for undertaking a CMT4A gene therapy project. Taysha and the CMTA will…
REPORT CONCEPTSPREADS72
…will continue to be moni- tored for one year after treatment. CMT4A mouse models have also been treated with the gene therapy and are currently being assessed to measure treatment…
2021_Spring_CMTA_Report
…depressing: Some great researchers were working on CMT, but because there were no pharmaceutical companies involved, the research wasn’t being translated to treatments. HOW DID WE GET FROM THERE TO…
Breakthrough Guide to Orthopedic Surgery for CMT
Download a PDF Copy The Charcot-Marie-Tooth Association (CMTA) is thrilled to share with you a first-of-its kind article entitled, “A Consensus Statement on The Surgical Treatment of Charcot-Marie-Tooth Disease.” Published…
CMTA Updates List of Neurotoxic Meds Potentially More Hazardous to CMT Patients
…than for people who do not have CMT. The reviewers emphasized the importance of not denying patients with CMT treatments that may prolong life expectancy for cancer or improve their…
Children/School
…your child’s treatment team, including his or her primary care physician, physiatrist and physical therapist. Is scoliosis a symptom of CMT? I’ve heard it affects school-age children and that it…