Taysha Letter to the GAN Community – 9.19.2023
…treatment of giant axonal neuropathy (GAN). This decision follows the receipt of feedback from the United States (U.S.) Food and Drug Administration (FDA) regarding a registrational path for TSHA-120. FDA…
Audited Financials
…information regarding CMT disorders. The Association encourages, promotes and supports research into the cause, treatment and cure of CMT disorders. The Association also facilitates education and support for persons affected…
CELEBRATING 2023
…and committed investments of $5,000,00 in research dedicated to finding effective treatments and ultimately a cure for Charcot-Marie-Tooth disease. Support for Natural History Studies Drives Clinical Trial Readiness: In 2023,…
CMTA_2019_Audited_Financial_Statements
…the healthcare community and the general public, and to be a leading source of information regarding CMT disorders. The Association encourages, promotes and supports research into the cause, treatment and…
Sample Press Release
…for a treatment for CMT, putting together a group of top-flight researchers and experts and directly funding their work. CMTA launched the Strategy to Accelerate Research, or STAR, in 2008…
Type1_Research_Developments_6-2020
As part of this multi-pronged approach to identifying novel treatments for demyelinating CMT, the CMTA is supporting several promising therapeutic opportunities in collaboration with more than a dozen key partners:…
Walk4CMT_Local_Day_of_Sponsorship_Template
…research for the types of CMT that affect approximately 90% of all people with CMT. We are aggressively fighting to find a pharmaceutical treatment, and, ultimately, a cure for all…
Ask the Expert
The CMTA has compiled a list of previously-asked member questions that have been answered by our CMT experts. You can browse these categories or use the site search function to…
CMTA_2014_Form_990
…drug testing in a transgenic rat model aimed at developing diagnostic applications and/or a pharmacological treatment of CMT1A disease. Region: Europe (d) Purpose of Grant: To conduct experimental therapy trial…
CMTA_2016-2017_Audited_Financial_Statements
…of information regarding CMT disorders. The Association encourages, promotes and supports research into the cause, treatment and cure of CMT disorders. The Association also facilitates education and support for persons…