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Gene Therapy for CMT1A, 1B, and X1: Progress in Nanoparticles
…the use of nanoparticles to deliver gene therapies directly to Schwann cells to treat CMTX1 (aka CMTX1, CMTX), the second most common type of CMT. This research focuses on using…
CMTA-STAR Advisory Board Member Dr. D’Antonio Publishes in Brain, Identifies Potential Therapeutic Target for CMT1B
…therapeutic target not only for CMT1B but also for other demyelinating forms of CMT, including CMT1A and CMT1E. In CMT1B, mutations in the MPZ gene can cause Schwann cells, which…
Gene Therapy Advances for CMT4J, CMT4A and GAN
…CMT, Giant Axonal Neuropathy (GAN), CMT4J, and CMT4A. The treatment for GAN has been in human clinical trials since 2015, the work for CMT4J is moving toward a human clinical…
The Summer 2021 CMTA Report
…Grants to Researchers Prepping for CMT1X, CMT2A Clinical Trials Interim Analysis Shows Sustained Benefits of PXT3003 for CMT1A Patients Seeking Participants for Biomarker Study It’s Time to Dance 4 CMT!…
Pete Foley Joins CMTA Board of Directors
Glenolden, PA, June 21, 2021—The Charcot-Marie-Tooth Association (CMTA), the national patient advocacy organization leading CMT research, today announced the appointment of Pete Foley to its Board of Directors. Originally from…
The Differences Between Charcot-Marie-Tooth Disease and Muscular Dystrophy (MD): An Overview
…No, CMT is not a form of MD. Although CMT shares many symptoms with the many forms of MD, CMT is a disease of the peripheral nerves and MD is…
Preguntas Frecuentes
…Tooth. ¿Hay algún tratamiento para CMT? No hay tratamientos conocidos que detenga o disminuya la progresión del CMT, pero la CMTA está financiando investigaciones para encontrar tratamientos. La terapia física,…
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CMTA Appoints Science and Technology Veteran, Patricia Verduin, PhD, to the Board of Directors
The Charcot-Marie-Tooth Association (CMTA), the largest philanthropic funder of Charcot-Marie-Tooth disease (CMT) research aimed at bringing treatments and a cure to patients, is pleased to announce the appointment of a…