Type 1 CMT Gene Therapy Project Now Underway

…Accelerate Research (STAR) brings top researchers together with pharmaceutical and biotechnology partners to accelerate scientific breakthroughs. STAR has one goal: to accelerate the development of treatments for CMT. Both research

STAR Advisory Board

…soundness of the research strategy. The progress of research teams, recommending changes in research strategies as needed. The Therapy Expert Board (TEB) evaluates the translational quality of ongoing and proposed…

CMT Type 2

…metabolic engines of the cells. Research on CMT Type 2A Type 2A2B CMT2A2B is the recessive form of CMT2A. Historically, KIF1B was originally published as causing CMT2A. That turned out…

CMTA-STAR Awards $354,826 for CMT Clinical Trial

…consolidated under the banner of STAR—which brings together the world’s largest network of biotech research partners, research scientists, clinicians and patients—and funds more CMT grants than any other philanthropic organization…

Help CMTA Develop Clinical Trials in a Dish

…they can become cells with specialized functions. Stem cells collected from CMT patients are an important tool for CMT research. They can be turned into neurons and glia, cell types…

Development of Treatments for CMT2D

…support the CMTA’s research efforts and enable expanded partnerships with world leading research laboratories, please consider making a donation in support of the CMTA’s Strategy to Accelerate Research. Published: June…

CMTA Announces New Center of Excellence in Canada

…care and research, becoming a permanent staff member in 2019. His clinical and translational research centers on congenital myopathies and spinal muscular atrophy (SMA). Dr. Gonorazky co-leads a national effort…

CMTA 2024 Year in Review Magazine

…to our community’s dedication, CMTA raised over $4.2 million to drive research and support programs that improve lives today while creating hope for tomorrow. Together, we are accelerating research and…