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CMTAfall2022web
CMTAfall2022web
2019_Summer_CMTA_Report
2019_Summer_CMTA_Report
CMTA Updates List of Neurotoxic Meds Potentially More Hazardous to CMT Patients
…Systematic Review. J Peripher Nerv Syst. 2023 May 30. doi: 10.1111/jns.12566. Epub ahead of print. PMID: 37249082. About the CMTA The CMTA is the leading patient advocacy organization driving CMT…
From Gene Discovery to Gene Editing: Closing the Diagnostic Gap and Developing CRISPR/Cas9 Capabilities in CMT
…work has led to the discovery of more than 25 genes in recent years, including the CADM3 (CMT2GG), COQ7 (dHMN-COQ7), ITPR3 (CMT1J), and SORD (CMT-SORD) genes. This program has a…
Type 1 CMT Gene Therapy Project Now Underway
…their behalf. To learn more about the CMTA, please visit www.cmtausa.org. Media contacts: Mary Fiance Director, Public Relations and Communications, MDA (646) 992-2908 mfiance@mdausa.org Marcia Semmes Media Relations, CMTA marcia@cmtausa.org…
Gene Replacement Therapy in CMT4 Subtypes
…using a model replicating CMT4A. If successful, this approach could serve as a template for treating other types of CMT, such as CMT4B1 and CMT4D. “Recent advances in developing desirable…
Type 1 CMT Gene Therapy Project Now Underway
…their behalf. To learn more about the CMTA, please visit www.cmtausa.org. Media contacts: Mary Fiance Director, Public Relations and Communications, MDA (646) 992-2908 mfiance@mdausa.org Marcia Semmes Media Relations, CMTA marcia@cmtausa.org…
CMT1X Research
…therapy for not only CMT1X but also other demyelinating forms of CMT (CMT1A and CMT4C). The CMTA convened a workshop with some of the world’s top gene therapy experts to…