CMT4 Research
…to advance research for CMT. Support CMT Research View the projects currently active or recently completed in the CMT4 drug development pipeline. CMT4 RESEARCH PROJECTS CMT4A Research CMT Type 4A…
The CMTA Is Accelerating Research Through Gene Therapy
…two mouse models of CMT: CMT1X and CMT4C. He is also extending his efforts to develop novel therapies for CMT1A. Dr. Harper has worked extensively in muscular dystrophy and is…
Alliance Partner NMD Pharma A/S Launches Phase II SYNAPSE-CMT Trial with First Patient Dosed at CMTA Center of Excellence
The Charcot-Marie-Tooth Association (CMTA) congratulates CMTA-STAR Alliance Partner NMD Pharma A/S (NMD Pharma) on initiating its Phase II SYNAPSE-CMT trial. This significant milestone reflects a shared commitment to advancing therapeutic…