CMTA and Taysha Gene Therapies Announce Collaboration for CMT4A
…100 different gene mutations causing CMT. Most people (90%) have one of four types of CMT: CMT 1A (PMP22); CMT 1B (MPZ); CMT 2A (MFN2) and CMT 1X (GJB1). It…
CMTA-STAR Awards Researcher $98,985 For CMT1A Project
…and CMT 1X (GJB1). It is estimated that CMT affects 3+ million people worldwide, regardless of gender, race, or ethnicity. More information can be found at https://www.cmtausa.org/understanding-cmt/what-is-cmt About the CMTA…
CMTA-STAR Awards $354,826 for CMT Clinical Trial
…CMT. Most people (90%) have one of four types of CMT: CMT 1A (PMP22); CMT 1B (MPZ); CMT 2A (MFN2) and CMT 1X (GJB1). It is estimated that CMT affects…
STAR: Our CMT Research Strategy
…more about how the CMT is accelerating research for Demyelinating and Axonal forms of CMT READ MORE: DEMYELINATING CMT ⟶ READ MORE: AXONAL CMT ⟶ Last Updated: November 12, 2024…
2021_Spring_CMTA_Report
CMT2A Research
CMT2A CMT2A is caused by dominant mutations in Mitofusin 2 (MFN2). The STAR team has developed two excellent rat models for CMT2A which are being made available to the research…
NMD Pharma Receives FDA Approval to Initiate Phase II Clinical Trial of NMD670 in CMT Patients
…clinical trial for their investigational drug, NMD670, in patients with Charcot-Marie-Tooth disease (CMT). This trial, named SYNAPSE-CMT, marks a significant milestone in the journey towards finding effective treatments for CMT….
CMTA-STAR Research for Axonal Forms of CMT
…in-depth conversation about STAR please reach out to Jeana Sweeney, Chief Engagement and Gift Officer: jeana@cmtausa.org. Support CMT Research READ MORE ABOUT CMTA-STAR RESEARCH FOR AXONAL TYPES OF CMT CMT…