Simply CMT Podcast Episode 2: Jonah Berger
…journey living with CMTX, the impact of CMTA’s Youth and Young Adults Programs, and how Camp Footprint empowers kids with Charcot-Marie-Tooth disease (CMT). Don’t forget to like, comment, and subscribe…
Breakthrough in CMT1A Research: Community Efforts Drive Success of Dental Stem Cell Model
…for future drug screening and treatment development beyond CMT1A, including CMT1E, HNPP, CMTX1 (aka CMT1X, CMTX), CMT2A, CMT2C, CMT2T, and CMT4A—the additional subtypes from which donations were received. Register With…
CMTA-STAR Alliance Partner Actio Biosciences Receives FDA Orphan Drug Designation and Rare Pediatric Disease Designation for Their Treatment in Development for CMT2C
…designation (RPDD) designation from the FDA for ABS-0871, a TRPV4 inhibitor for treating CMT2C. This achievement represents a crucial step forward for CMT2C patients and the CMT community. “We are…
CMTA and Pharnext Enter Biomarker Research Collaboration
…About CMTA The CMTA is aggressively leading the fight to fund the development of treatments and, ultimately, a cure for CMT. Through its Strategy to Accelerate Research (STAR), the CMTA…
CMTA Lunch & Learn: Exercise & Staying Active
06/27/2024 @ 12:00 pm – 1:00 pm – CMTA’s virtual Lunch and Learn Community Event Series returns via Zoom on Thursday, June 27 with Exercise and Staying Active with CMT. Learn about the importance of staying active and embracing exercise in our daily lives while focusing on adaptive forms of exercise, exploring unique ways to stay active, and discussing the importance of movement. […]
Nervosave: Shaping the Future of Genetic Therapy for CMT1A
…is looking for: Individuals with genetically confirmed CMT1A Symptomatic individuals with a confirmed family history of CMT1A Parents of children with genetically confirmed CMT1A What’s Involved? Participation involves completing a…
A New Treatment for CMT1A
…associations, including the CMTRF and the CMTA. DTx appreciates patient participation in natural history studies, such as the ongoing observational study ACT-CMT (Accelerate Clinical Trials in Charcot-Marie-Tooth Disease), which support…
CMTA Unveils Updated Logo
…20 pharmaceutical and biotechnology partners, the world’s top CMT scientists collaborating through STAR, and a community powering our efforts, the CMTA is leading the way to a world without CMT….
CMTA and ToolGen Announce CMT1A Collaboration
CMTA and ToolGen Announce Collaboration to Develop Potential Treatment for CMT1A Using Gene Therapy (Glenolden, PA, October 7, 2021) The Charcot–Marie–Tooth Association (CMTA), the largest philanthropic funder of CMT research…
CMT-SORD: Bringing the Science Down to Earth | Shooting Star Ep. 3
…and enthusiasm with important updates on CMTA programs, research, and community impact. In this episode, we dive into CMT-SORD, a unique form of Charcot-Marie-Tooth disease (CMT) linked to mutations in…