Accelerating Genetic Therapy for CMT4B1: A CMTA Research Update
…$380,000 CMTA Strategy To Accelerate Research (CMTA-STAR) investment is part of a broader effort to accelerate genetic therapies for less common, severe forms of CMT, including CMT4B2 and CMT4B3. Targeting…
DNA-Based Therapeutics: A Promising Future for CMT2E Treatment
…have made significant progress in DNA-based therapeutics. Their groundbreaking work targets the fundamental genetic cause of CMT2E. CMT2E is an axonal CMT (CMT2). Several different autosomal dominant mutations of the…
Mebane Walk4CMT
09/20/2025 @ 9:00 am – 12:00 pm – Whether you walk, run or roll, we invite you to join us at the 2025 Mebane Walk4CMT for a nice and enjoyable day. Come out and connect with other people with Charcot-Marie-Tooth (CMT), families, and local companies while fundraising for a cure. Fun for all the whole family! About Walk 4 CMT Walk 4 CMT […]
MDA and CMTA Partner to Advance Treatments and Care for Charcot-Marie-Tooth Disease
…kids and adults affected by CMT, medical professionals and the public. The partnership represents a key step in MDA’s commitment to form strategic alliances with for- and non-profit organizations. CMT…
CMT Respiratory Impairment Final
2023 CMTA-STAR Celebrating our Collective Achievements
…CMTA is currently funding the development of genetic therapy across all major CMT subtypes! This includes projects supporting gene editing for demyelinating (Type 1) CMTs and a genetic therapy for…
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Accelerate Clinical Trials in Charcot-Marie-Tooth Disease (ACT-CMT)
…Neuropathy Limitation Scale) that explore how CMT1A affects you Standardized questions and clinical examination of your CMT, known as the CMT Exam Score (CMTES) CMT Functional Outcome Measure (CMT-FOM) which…