The 2019 Spring CMTA Report
Clinical Trials: A Primer! In addition to our regular features, read about “A Clinical Trial for Caroline,” fast tracking and more.Read more ...
CMTA Unveils Updated Logo
For more than 35 years, the CMTA has supported the CMT community and invested in the most promising treatment-oriented research. The CMT community has been with us every step of the way. That is why, ...Read more ...
Type 1 CMT Gene Therapy Project Now Underway
CMTA and MDA Co-Fund Proof-of-Concept Study Using AAV Vector to Deliver Gene Replacement Therapy in X-linked Charcot-Marie-Tooth DiseaseRead more ...
Rare Disease Day 2-28-2019: Read Our Stories
Caroline’s journey with a rare and serious form of CMT began when she was just 9 months old. Today, a cure for Caroline may open the door to treatments and a cure for CMT!Read more ...
Research Project Identifies New Types of CMT
Dr. Stephan Züchner at the University of Miami is spearheading an ambitious project to identify new disease-causing mutations in patients.Read more ...