Taxonomy

Data Shows Benefit with PXT3003 in Patients with CMT1A

New Data from the Open-Label PLEO-CMT-FU Trial Shows Sustained Benefit

Orphan Drug Designation for TSHA-120 for Treatment of GAN

Taysha Gene Therapies Receives Orphan Drug Designation from the European

The CMTA Earns a Perfect Rating From Charity Navigator

The Charcot-Marie-Tooth Association Earns a Perfect Rating From Charity Navigator

Initiation of Registrational Phase 2/3 Study of AT-007 in SORD Deficiency

Applied Therapeutics Announces Initiation of Registrational Phase 2/3 Study of

CMTA Seed Money Draws NIH Support For Type 2 Gene Editing

CMTA Seed Money Draws NIH Support For Type 2 Gene

CMTA-STAR Awards $354,826 for CMT Clinical Trial

CMTA-STAR Awards $354,826 for CMT Clinical Trial (Glenolden, PA, December

CMTA-STAR Awards Researcher $98,985 For CMT1A Project

CMTA-STAR Awards Researcher $98,985 For CMT1A Project Using Dental Pulp

CMTA and Taysha Gene Therapies Announce Collaboration for CMT4A

CMTA and Taysha Gene Therapies Announce Collaboration for CMT4A (Glenolden,

CMTA and Applied Therapeutics Announce Collaboration for CMT-SORD

CMTA and Applied Therapeutics Announce Collaboration for CMT-SORD (Glenolden, PA,

Taysha Gene Therapies & CMTA Collaborate to Increase Genetic Testing Access for Giant Axonal Neuropathy (GAN)

Taysha Gene Therapies Announces Sponsored Genetic Testing for Giant Axonal