Research | Charcot-Marie-Tooth Association



STAR, the CMTA’s research initiative, was created with one goal: to find treatments to slow, stop or reverse the progression of CMT.  Working with investigators and scientists chosen from an international body of the world’s most accomplished medical pioneers, STAR is leading CMT research. The STAR program’s success is due to the willingness of scientists working in their areas of expertise to come together as a team to advance CMT research, sharing and communicating ideas, discoveries and findings.  Scientists sharing their successes and failures every month is what sets the STAR program apart from any other CMT-related research effort.

CMT1A Research Breakthrough

CMT1A Research Breakthrough!

Scientists at Ionis Pharmaceuticals, in collaboration with the Charcot-Marie-Tooth Association, have identified a promising early-stage therapeutic approach with antisense technology for CMT Type 1A (CMT1A), the most common form of the disease, accounting for half of all cases. Read more …